National PKU News
www.pkunews.org

PKU Research

• BioMarin’s Kuvan is First FDA-Approved Drug for PKU
  from National PKU News, Volume 20, Number 1, Spring/Summer 2008

• The FDA Should Not have Approved Kuvan
  from National PKU News, Volume 20, Number 1, Spring/Summer 2008

• Message from the Editor of National PKU News regarding Kuvan’s FDA Approval
  from National PKU News, Volume 20, Number 1, Spring/Summer 2008

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• International Meeting Highlights Potential Breakthrough Treatments for PKU

• Meeting in Japan Highlights Research on NeoPhe in the Treatment of PKU

• Using Glycomacropeptide (GMP) for PKU Diet Treatment

• The Long Road to Developing a PKU Therapeutic

• BioMarin Announces that Kuvan Significantly Increases Phe Tolerance in BH4-Responsive PKU

• Expanded Access Program for Sapropterin Begins Nationwide

• More Information on the Expanded Access Program

• Should I Try the New Drug? Weighing Risks versus Benefits

• Essential Fatty Acids and the PKU Diet

• Using Large Neutral Amino Acids for PKU: A View from "Down Under"

• Questions and Answers about LNAA Use

• ADHD and PKU

• Fatty Acid Status Of Metabolic Patients: To Supplement Or Not To Supplement?

• BioMarin Forges Ahead with Research On PKU Diet Alternatives
• Will Tetrahydrobiopterin Have A Role In PKU Treatment?

• Results from the International Maternal PKU Study

• Can a Pill Partially Replace the PKU Diet?
  • Our Experience with PreKUnil Tablets
  • Commentary on PreKUnil Tablet Use
  • PreKUnil Tablets: Let's Be Cautious

• Ohio Conference Draws People from Thirty States and Seven Other Countries
  • Brain Phe and PKU
  • Phenylketonuria: The Irish Experience
  • ADHD and PKU

• Report on the Latest Scientific Developments in PKU

• Study Shows Long-Term Beneficial Effects of the PKU Diet, Even for Late-Diagnosed Persons

• Update on Phenylase Research

• Inborn Errors of Metabolism: the Search for Alternate Treatments Goes On